An overview of microRNAs ☆
Basic biology and therapeutic implications of lncRNA ☆
DNA and RNA derivatives to optimize distribution and delivery ☆
Cellular uptake and intracellular trafficking of oligonucleotides ☆
Pharmacokinetics, biodistribution and cell uptake of antisense oligonucleotides ☆
Delivery of therapeutic oligonucleotides with cell penetrating peptides ☆
Delivery of oligonucleotides with lipid nanoparticles ☆
Bioconjugates for targeted delivery of therapeutic oligonucleotides ☆
Antisense oligonucleotides in therapy for neurodegenerative disorders ☆
Exon skipping therapy for Duchenne muscular dystrophy ☆
Preclinical and clinical development of siRNA-based therapeutics ☆,☆☆