Cover Image, Volume 172C, Number 4, December 2016
Table of Contents, Volume 172C, Number 4, December 2016
Publication schedule for 2016
Treatment of genetic disorders—A vision coming into focus
Alternative designs for clinical trials in rare diseases
Emerging cellular and gene therapies for congenital anemias
Gene and cell‐based therapies for inherited retinal disorders
Pharmacological and biological therapeutic strategies for osteogenesis imperfecta
Angelman syndrome
Somatic overgrowth disorders of the PI3K/AKT/mTOR pathway & therapeutic strategies
Chromosome therapy